Celebrating Dr. Marilyn Hughes Gaston, a leading researcher on Sickle Cell disease and the first Black woman to be appointed director of the Health Resources and Services Administration’s Bureau of Primary Health Care...
This is a great honor but where is the cure? Just like HIV. Nobody wants to cure anything. They continue to make stronger meds for the Pharmacy companies to make money. LOLO
She is a pioneer. Her work opened the door for the cure that is being used today. Recent advancements in gene therapy, specifically the FDA-approved treatments Casgevy and Lyfgenia, offer promising cures for sickle cell disease, marking a significant breakthrough in medical treatment. Gene Therapy Approvals Casgevy: This is the first FDA-approved treatment utilizing CRISPR gene-editing technology. It works by modifying a patient's own blood stem cells to remove the gene responsible for sickle cell disease. The modified cells are then transplanted back into the patient, where they produce healthy red blood cells that do not sickle. This therapy is approved for patients aged 12 and older and is considered a game-changer in the treatment landscape for sickle cell disease. 2 Lyfgenia: Another gene therapy approved by the FDA, Lyfgenia uses a lentiviral vector to modify blood stem cells, enabling them to produce a type of hemoglobin that reduces the risk of sickling. This treatment is also approved for patients aged 12 and older and represents a significant advancement in the management of sickle cell disease.
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This is a great honor but where is the cure? Just like HIV. Nobody wants to cure anything. They continue to make stronger meds for the Pharmacy companies to make money. LOLO
I appreciate the black history facts through the year. Salute.
Salute!
She is a pioneer. Her work opened the door for the cure that is being used today.
Recent advancements in gene therapy, specifically the FDA-approved treatments Casgevy and Lyfgenia, offer promising cures for sickle cell disease, marking a significant breakthrough in medical treatment.
Gene Therapy Approvals
Casgevy: This is the first FDA-approved treatment utilizing CRISPR gene-editing technology. It works by modifying a patient's own blood stem cells to remove the gene responsible for sickle cell disease. The modified cells are then transplanted back into the patient, where they produce healthy red blood cells that do not sickle. This therapy is approved for patients aged 12 and older and is considered a game-changer in the treatment landscape for sickle cell disease.
2
Lyfgenia: Another gene therapy approved by the FDA, Lyfgenia uses a lentiviral vector to modify blood stem cells, enabling them to produce a type of hemoglobin that reduces the risk of sickling. This treatment is also approved for patients aged 12 and older and represents a significant advancement in the management of sickle cell disease.
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